DISEASE SCANNER

Global Incurable Diseases Tracker

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Cancer

Chronic Myeloid Leukemia

HIGH SEVERITY

A myeloproliferative neoplasm characterized by the Philadelphia chromosome (t(9;22)) creating the BCR-ABL fusion gene, leading to constitutively active tyrosine kinase. Chronic phase is indolent; without treatment progresses to accelerated phase and blast crisis.

Global Affected

150.0K

Countries

111

Symptoms

Often asymptomatic (chronic phase)
Fatigue
Weight loss
Night sweats
Abdominal fullness (splenomegaly)
Early satiety
Left upper quadrant pain
Easy bruising/bleeding
Fever

Treatment Options

Imatinib
Dasatinib
Nilotinib
Bosutinib
Ponatinib (T315I mutations)
Asciminib (STAMP inhibitor)
Allogeneic stem cell transplant (blast crisis or TKI failure)
Omacetaxine

Risk Factors

1Age (median 64)
2Male gender
3Radiation exposure
4BCR-ABL fusion gene
5No other well-established risk factors

Diagnostic Methods

  • 1Complete blood count
  • 2Peripheral blood smear
  • 3Bone marrow biopsy
  • 4Cytogenetics (Philadelphia chromosome)
  • 5FISH for BCR-ABL
  • 6Quantitative PCR for BCR-ABL transcript
  • 7Mutation testing (if TKI resistance)

Prognosis

With TKI therapy, 10-year survival approaches 90% (similar to general population). Deep molecular response (MR4.5) allows consideration of treatment-free remission in 40-60%. Blast crisis without treatment median survival 3-6 months.

Prevention

  • No known prevention
  • Avoid unnecessary radiation exposure
  • Early detection through routine blood work

Research Status

Tyrosine kinase inhibitors (TKIs) transformed CML from fatal to chronic disease. Imatinib first, now second/third generation TKIs (dasatinib, nilotinib, bosutinib, ponatinib) with deeper responses. Treatment-free remission possible in selected patients.

Sources

  • https://www.cancer.gov/
  • https://www.hematology.org/education/patients
  • https://www.ncbi.nlm.nih.gov/books
  • https://rarediseases.org/rare-diseases

Medical Disclaimer

This information is for educational purposes only. Always consult healthcare professionals for medical advice, diagnosis, and treatment.