DISEASE SCANNER

Global Incurable Diseases Tracker

Back to Globe
Genetic Disorder

Leber Hereditary Optic Neuropathy (LHON)

HIGH SEVERITY

A mitochondrial disorder causing sudden, painless vision loss in young adults, typically males. Caused by mutations in mitochondrial DNA (MT-ND1, MT-ND4, MT-ND6, MT-ND4L). Usually affects one eye first, then the other within weeks to months.

Global Affected

100.0K

Countries

15

Symptoms

Painless central vision loss
Central scotoma
Dyschromatopsia
Visual acuity 20/200 or worse
Swollen optic disc (acute)
Optic atrophy (chronic)

Treatment Options

Genetic counseling
Supportive care
Symptom management
Enzyme replacement (if applicable)
Physical therapy
Regular monitoring
Multidisciplinary care

Risk Factors

1Family history
2Genetic mutations
3Consanguinity
4Advanced paternal age
5Ethnic predisposition

Diagnostic Methods

  • 1Genetic testing
  • 2Clinical evaluation
  • 3Family history assessment
  • 4Specialized laboratory tests
  • 5Imaging studies
  • 6Biopsy (if applicable)

Prognosis

Acute sequential vision loss over weeks to months, then chronic stable blindness. Spontaneous recovery occurs in 10-20% of cases, more commonly in females. Vision typically stabilizes at 20/200 or worse in affected eyes. Idebenone may accelerate recovery in some patients. Avoiding smoking and alcohol (mitochondrial toxins) is important. Genetic counseling essential as maternal inheritance pattern. Risk to offspring of carrier mother is 50%.

Prevention

  • Genetic counseling
  • Carrier screening
  • Prenatal diagnosis
  • Preimplantation genetic diagnosis
  • Family planning

Research Status

Idebenone (antioxidant) may help if started early. Gene therapy (GS010) in clinical trials. Vision rehabilitation. Avoidance of triggers (smoking, alcohol). Spontaneous recovery in some (especially m.3460G>A).

Sources

  • https://www.ncbi.nlm.nih.gov/books/NBK1116
  • https://medlineplus.gov/genetics
  • https://rarediseases.org

Medical Disclaimer

This information is for educational purposes only. Always consult healthcare professionals for medical advice, diagnosis, and treatment.