DISEASE SCANNER

Global Incurable Diseases Tracker

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Genetic Disorder

Hereditary Hemochromatosis

MODERATE

An inherited disorder causing excessive iron absorption and deposition in organs, leading to organ damage. Most common form caused by HFE gene mutations (C282Y). Called 'bronze diabetes' historically due to skin pigmentation and diabetes.

Global Affected

1.5M

Countries

17

Symptoms

Fatigue
Joint pain
Abdominal pain
Skin bronzing
Diabetes
Liver disease/cirrhosis
Heart problems
Erectile dysfunction
Hypothyroidism

Treatment Options

Genetic counseling
Supportive care
Symptom management
Enzyme replacement (if applicable)
Physical therapy
Regular monitoring
Multidisciplinary care

Risk Factors

1Family history
2Genetic mutations
3Consanguinity
4Advanced paternal age
5Ethnic predisposition

Diagnostic Methods

  • 1Genetic testing
  • 2Clinical evaluation
  • 3Family history assessment
  • 4Specialized laboratory tests
  • 5Imaging studies
  • 6Biopsy (if applicable)

Prognosis

Excellent with phlebotomy treatment. Normal life expectancy if diagnosed before organ damage. Cirrhosis and diabetes preventable. Regular screening of first-degree relatives recommended.

Prevention

  • Genetic counseling
  • Carrier screening
  • Prenatal diagnosis
  • Preimplantation genetic diagnosis
  • Family planning

Research Status

Therapeutic phlebotomy to maintain ferritin <50 ng/mL. Iron chelation for selected patients. Early diagnosis prevents organ damage. Genetic testing for family members. Liver transplant for end-stage liver disease.

Sources

  • https://www.ncbi.nlm.nih.gov/books/NBK1116
  • https://medlineplus.gov/genetics
  • https://rarediseases.org

Medical Disclaimer

This information is for educational purposes only. Always consult healthcare professionals for medical advice, diagnosis, and treatment.