DISEASE SCANNER

Global Incurable Diseases Tracker

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Genetic Disorder

Dent Disease

HIGH SEVERITY

An X-linked recessive renal tubular disorder caused by CLCN5 or OCRL1 mutations. Characterized by low-molecular-weight proteinuria, hypercalciuria, nephrocalcinosis, kidney stones, and progressive renal failure. Often presents in childhood.

Global Affected

25.0K

Countries

15

Symptoms

Low-molecular-weight proteinuria
Hypercalciuria
Nephrocalcinosis
Kidney stones
Rickets (some)
Short stature
Progressive renal failure
Hypophosphatemia

Treatment Options

Genetic counseling
Supportive care
Symptom management
Enzyme replacement (if applicable)
Physical therapy
Regular monitoring
Multidisciplinary care

Risk Factors

1Family history
2Genetic mutations
3Consanguinity
4Advanced paternal age
5Ethnic predisposition

Diagnostic Methods

  • 1Genetic testing
  • 2Clinical evaluation
  • 3Family history assessment
  • 4Specialized laboratory tests
  • 5Imaging studies
  • 6Biopsy (if applicable)

Prognosis

Progressive kidney disease. 30-80% develop ESRD by age 30-50. Rickets responsive to vitamin D. Regular monitoring essential for early intervention.

Prevention

  • Genetic counseling
  • Carrier screening
  • Prenatal diagnosis
  • Preimplantation genetic diagnosis
  • Family planning

Research Status

Supportive care. Thiazide diuretics may reduce calciuria. Citrate supplements. No specific cure. Monitoring for ESRD. Genetic counseling. Most males progress to ESRD by age 30-50.

Sources

  • https://www.ncbi.nlm.nih.gov/books/NBK1116
  • https://medlineplus.gov/genetics
  • https://rarediseases.org

Medical Disclaimer

This information is for educational purposes only. Always consult healthcare professionals for medical advice, diagnosis, and treatment.